Effective Cystine Level Lowering with Oral Administration of Delayed-Release Cysteamine Bitartrate in Young Infants with Cystinosis

Mallory Mandel, Boston Children's Hospital, Boston, MA, United States; Avram Traum, Boston Children's Hospital, Boston, MA, United States; Deborah R.. Stein, Boston Children's Hospital, Brookline, MA, United States