Efficacy of DNM2 Reduction and Mesenchymal Stem Cell-Derived Extracellular Vesicles in SPEG Deficiency

Sara Ali, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Victtoria O. Ardellini, Holtz Children's Hospital Jackson Memorial Hospital, Sunny Isles Beach, FL, United States; Qifei Li, University of Miami Miller School of Medicine and Holtz Children's Hospital, Miami, FL, United States; Shiyu Luo, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Haoyue sheng, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Aisha Khan, University of Miami, Miami, FL, United States; Yee-Shuan Lee, University of Miami, Miami, FL, United States; Huijun Yuan, University of Miami Leonard M. Miller School of Medicine, miami, FL, United States; Shu Wu, University of Miami, miami, FL, United States; Pankaj Agrawal, Holtz Children's Hospital Jackson Memorial Hospital, Miami, FL, United States